Pediatric Rare Disease Clinical Trials � Challenges and Solutions

Vineet Bhatt28 Sep, 2024Technology

Clinical trials (CT) are the long and complex processes for bringing novel medical products to patients through the regulatory process of evaluating the safety and efficacy of treating specific medical conditions in humans. In addition to the challenges associated with adult clinical trials, there are unique challenges in conducting pediatric clinical trials. The challenges facing pediatric CTs are particularly severe in the case of rare diseases that affect only a small subset of the population.